GEN TERAPIYASINING ZAMONAVIY RIVOJLANISHLARI, UNING IMKONIYATLARI VA AHAMIYATI, GENETIK KASALLIKLARNI DAVOLASHDAGI YANGI YONDOSHUVLAR.
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Keywords

Gen terapiyasi, genetik kasalliklar, CRISPR, gen tahriri, DNK, RNK, tashuvchi vektor, individual davolash, biotexnologiya, irsiy muammolar.

Abstract

Ushbu maqolada gen terapiyasining zamonaviy rivojlanish bosqichlari, ilm-fan va amaliy tibbiyotdagi ahamiyati, shuningdek, genetik kasalliklarni davolashda qo‘llanilayotgan yangi texnologiyalar ko‘rib chiqiladi. CRISPR-Cas9, somatik va germinal hujayralarga ta’sir ko‘rsatish usullari, virusli va virus bo‘lmagan tashuvchi sistemalar, shuningdek, individual davolash yondoshuvlari tahlil qilinadi. Gen terapiyasi inson genetik kodini to‘g‘rilash orqali ilgari davolab bo‘lmas deb hisoblangan irsiy kasalliklarni samarali davolash imkonini bermoqda.

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